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Events
October 20-21, 2025 - Cambridge, MA Join us for our annual Nano-rare patient Colloquium. This event is free to attend — register today!
Past Events
October 30-31, 2024 - Cambridge, MA Recap the 2024 Nano-rare Patient Colloquium
July 11, 2024 - Chicago, IL The North America Rare Disease Summit brings together leading researchers, healthcare professionals, patient advocates, policymakers, industry experts, and rare disease patients and families.
April 23-25, 2024 - Boston, MA The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers.
October 12, 2023 - Cambridge, MA Rewatch the first ever Nano-rare patient Colloquium held at Biogen headquarters.
June 20-21, 2023
Massachusetts Institute of
Technology - Boston, MA
We are continuously developing new partnerships, new treatments, and solutions to those with nano-rare diseases. Contact us to learn more about our organization.

We cannot do
this alone
Together we are changing the world—
one patient at a time
We hope that you join us on this journey to discover, develop and provide individualized antisense medicines for free for life for nano-rare patients. The ultimate personalized medicine approach – for free, for life.
Follow us on social for updates on our latest efforts