Susannah’s Progress: Two Years of ASO Treatment
with Dr. Jennifer Bain and Luke Rosen
Sneak Peek of the 2024 Nano-rare Patient Colloquium
Brady Huggett interviews Stan Crooke
Knowledge is Power: Part 2
The [...]
Knowledge is Power: Part 1
The [...]
The Building Blocks of What’s Possible
with David Butler, Ph.D.
Adopting a Rare Son
with Paul Compton
Ion Channel Mutations: The Complexities of Treatment
Arguably, the [...]
Why We Dose Intrathecally
Intrathecal administration [...]
Behind the ASO Design and Discovery
with Konstantina Skourti-Stathaki, Ph.D.
Best of the 2023 Nano-rare Patient Colloquium
Don't [...]
