Susannah’s Progress: Two Years of ASO Treatment
with Dr. Jennifer Bain and Luke Rosen
n-Lorem Publishes Recommendations for Treating Patients with Heterozygous Toxic Gain of Function Mutations
Article published in Nucleic [...]
Sneak Peek of the 2024 Nano-rare Patient Colloquium
Brady Huggett interviews Stan Crooke
Knowledge is Power: Part 2
The [...]
Knowledge is Power: Part 1
The [...]
The Building Blocks of What’s Possible
with David Butler, Ph.D.
Positive Clinical Observations from n-Lorem Treated, KIF1A Nano-rare Patient Published in Nature Medicine
Case study, published in [...]
