ASOs Drive Foundation’s Work to Develop Treatments for the World’s Rarest Diseases
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Why We Dose Intrathecally
Intrathecal administration [...]
Kuri’s Story: DRPLA
6 minutes
Behind the ASO Design and Discovery
with Konstantina Skourti-Stathaki, Ph.D.
Best of the 2023 Nano-rare Patient Colloquium
Don't [...]
North American Rare Diseases Summit 2024
July 11, 2024 - Chicago, IL The World Orphan Drug Congress brings together leading pharmaceutical and biotech companies, government and regulatory authorities, patient advocacy groups, payers, investors and solution providers.
The Hurdles of Insuring Patients with Nano-rare Mutations
with Alan Lotvin, M.D.
Anna’s Story of Hope and Help: FUS-ALS
with Sonja Kämpfer and Dr. Neil Shneider
CYTIVA PRESS RELEASE: Cytiva continues its support for n-Lorem Foundation
Donation will assist in [...]
